2024 Rome, Italy
Meeting information
Abstracts
Programme Item
Presenter
Abstract Category
Search Abstract
I-56 Gilles Tiraboschi
Population Pharmacokinetic and Pharmacodynamic Analyses of Olipudase alfa in Adult and Pediatric Patients with the rare Acid Sphingomyelinase Deficiency (Niemann-Pick) lysosomal storage disease
Wednesday 09:45-11:15